Thalassemia Reports | Free Full-Text | CRISPR Gene Therapy: A Promising One-Time Therapeutic Approach for Transfusion-Dependent β-Thalassemia—CRISPR-Cas9 Gene Editing for β-Thalassemia
Pediatric Thalassemia: Practice Essentials, Background, Pathophysiology
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Introductory Chapter: β-Thalassemia | IntechOpen
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
β-Thalassemia | Genetics in Medicine
Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Β-Thalassemias | NEJM
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
Frontiers | Genetic and Epigenetic Therapies for β-Thalassaemia by Altering the Expression of α-Globin Gene
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
IJMS | Free Full-Text | Thalassemia Intermedia: Chelator or Not?
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article - Cureus
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PDF] Current and future alternative therapies for beta-thalassemia major | Semantic Scholar
Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia: Molecular Therapy
Luspatercept for the treatment of β-thalassemia: from preclinical research to clinical practice and beyond | Future Rare Diseases
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Thalassaemia - The Lancet
Β-Thalassemias | NEJM
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
